Indication: Spinal Muscular Atrophy (SMA)
Use of AVXS-101 for treatment of a patient with Spinal Muscular Atrophy (SMA) Type 1
Sub-indication: Spinal Muscular Atrophy (SMA)
Study Type: Drug Study
Principal Investigator: Arpita Lakhotia, M.D.Norton Children's Neurology, affiliated with the UofL School of Medicine
Sponsor: Sponsor: AveXis Inc